Objectives of the Call:
- To advance the development of new therapeutic options with concrete benefits for patients living with rare diseases.
- To progress in orphan drug development due to well-prepared clinical trials and a multinational multicentre clinical trial with an appropriate number of patients.
- To develop a preliminary assessment of the potential economic and public health aspects of the new therapeutic option.
- To contribute to growth of SMEs involved in drug development.
- To contribute towards International Rare Diseases Research Consortium (IRDiRC) objectives
27 de Julio de 2016 a 10 de Abril de 2017